My wife, Jolandie, and I had a pretty good thing going back in our hometown of Mbombela, South Africa. By age 25, I had successfully owned and operated two reputable businesses, had a lovely home, and plenty of people we...

New approaches are needed for both prevention and treatment of squamous cell carcinoma (SCC) in patients with FA - approaches that have fewer and less severe side effects than chemotherapy and radiation therapy. The purpose of this Phase 2 study...

Hola FAmilia ?? my name is Mary-Beth. At this year’s FAdult Meeting in Chicago, we did something special one day. I took over FARF’s Facebook on the first day of the FAdult Meeting to share a little behind the scenes...

Why gene therapy? We know that Fanconi anemia (FA) is caused by defects in any one of 23 different genes called “FANC” genes. If we could somehow repair or replace these defective FANC genes, we could treat or prevent FA...