A novel treatment that uses gene therapy to correct a faulty gene in the stem cells of the recipient. Stem cells are obtained from the patient, grown and “corrected” in a laboratory, and then returned to the patient.
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To advance our commitment to mental health, FCF has partnered with Give An Hour (GAH), a national nonprofit dedicated to expanding access to no-cost mental health care and education.
If you asked me for a defining memory of our journey, it might surprise you. Some of my most cherished moments were the long hospital stays — the time I got to spend one-on-one with Hunsley, free from the distractions of the world.
We’re thrilled to share that Rena and Paul Rice, parents of two children with Fanconi anemia—Sydney (19) and Blake (25)—have made an extraordinary commitment to the FA community: a gift of $100,000 per year for the next three years to...